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Amedeo Smart
Independent Medical Education
Iwan V, Nadzemova O, Weiand M, Zibert A, et al. CRISPR/Cas9-mediated gene correction of Wilson disease H1069Q point mutation in patient-specific induced pluripotent stem cells. Gene Ther 2026 Apr 14. doi: 10.1038/s41434-026-00611.PMID: 41981235
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