Lee JWA, Huang H, Wang FS, Tay SKH, et al. Treatment Outcome of Risdiplam and Onasemnogene Abeparvovec in an Infant With Spinal Muscular Atrophy Dependent on Prolonged Invasive Ventilation. J Paediatr Child Health 2025 Sep 18. doi: 10.1111/jpc.70199.
PMID: 40965051