Agarwal R, Bertaina A, Soco C, Long-Boyle JR, et al. Irradiation- and busulfan-free stem cell transplantation in Fanconi anemia using an anti-CD117 antibody: a phase 1b trial. Nat Med 2025 Jul 22. doi: 10.1038/s41591-025-03817.
PMID: 40696207