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Amedeo Smart

Independent Medical Education


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Shneider NA, Harms MB, Korobeynikov VA, Rifai OM, et al. Antisense oligonucleotide jacifusen for FUS-ALS: an investigator-initiated, multicentre, open-label case series. Lancet 2025 May 22:S0140-6736(25)00513-6. doi: 10.1016/S0140-6736(25)00513.
PMID: 40414239


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