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Amedeo Smart
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Kuo KHM, Layton DM, Lal A, Vichinsky EP, et al. Long-term efficacy and safety of mitapivat in non-transfusion-dependent alpha- or beta-thalassaemia: An open-label phase 2 study. Br J Haematol 2025;206:1764-1773.PMID: 40394935
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