Gene therapy in children with AIPL1-associated severe retinal dystrophy: an open-label, first-in-human interventional study. Michaelides M, Laich Y, Wong SC, Oluonye N, et al. Lancet 2025;405:648-657.

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Amedeo Smart

Independent Medical Education

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Michaelides M, Laich Y, Wong SC, Oluonye N, et al. Gene therapy in children with AIPL1-associated severe retinal dystrophy: an open-label, first-in-human interventional study. Lancet 2025;405:648-657.
PMID: 39986747