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Amedeo Smart
Independent Medical Education
McMillan HJ, Baranello G, Farrar MA, Zaidman CM, et al. Safety and Efficacy of IV Onasemnogene Abeparvovec for Pediatric Patients With Spinal Muscular Atrophy: The Phase 3b SMART Study. Neurology 2025;104:e210268.PMID: 39804575
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