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Amedeo Smart
Independent Medical Education
Laugwitz L, Mechtler TP, Janzen N, Oliva P, et al. Newborn Screening and Presymptomatic Treatment of Metachromatic Leukodystrophy. N Engl J Med 2024 Sep 18. doi: 10.1056/NEJMc2407165.PMID: 39292923
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