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Amedeo Smart

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Laugwitz L, Mechtler TP, Janzen N, Oliva P, et al. Newborn Screening and Presymptomatic Treatment of Metachromatic Leukodystrophy. N Engl J Med 2024 Sep 18. doi: 10.1056/NEJMc2407165.
PMID: 39292923


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