Pramanik-Jonsson L, Borssen M, Vonlanthen S, Nilsson F, et al. Severe Thrombocytopenia Due to Bone Marrow Failure in Children With Dyskeratosis Congenita Does Not Respond to Eltrombopag Treatment: Case Series. J Pediatr Hematol Oncol 2024;46:57-62.
PMID: 37885072