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Amedeo Smart
Independent Medical Education
Michaelides M, Hirji N, Wong SC, Besirli CG, et al. First-in-Human Gene Therapy Trial of AAV8-hCARp.hCNGB3 in Adults and Children With CNGB3-associated Achromatopsia. Am J Ophthalmol 2023;253:243-251.PMID: 37172884
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