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Amedeo Smart

Independent Medical Education


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Zhao X, Lin Y, Liou B, Fu W, et al. PGRN deficiency exacerbates, whereas a brain penetrant PGRN derivative protects, GBA1 mutation-associated pathologies and diseases. Proc Natl Acad Sci U S A 2023;120:e2210442120.
PMID: 36574647


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