Kuo KHM, Layton DM, Lal A, Al-Samkari H, et al. Safety and efficacy of mitapivat, an oral pyruvate kinase activator, in adults
with non-transfusion dependent alpha-thalassaemia or beta-thalassaemia: an
open-label, multicentre, phase 2 study. Lancet 2022;400:493-501.
PMID: 35964609