Rescue of a lysosomal storage disorder caused by Grn loss of function with a brain penetrant progranulin biologic. Logan T, Simon MJ, Rana A, Cherf GM, et al. Cell 2021;184:4651-4668.

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Amedeo Smart

Independent Medical Education

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Logan T, Simon MJ, Rana A, Cherf GM, et al. Rescue of a lysosomal storage disorder caused by Grn loss of function with a brain penetrant progranulin biologic. Cell 2021;184:4651-4668.
PMID: 34450028