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Amedeo Smart
Independent Medical Education
Cromer MK, Camarena J, Martin RM, Lesch BJ, et al. Gene replacement of alpha-globin with beta-globin restores hemoglobin balance in beta-thalassemia-derived hematopoietic stem and progenitor cells. Nat Med 2021;27:677-687.PMID: 33737751
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