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Amedeo Smart
Independent Medical Education
Lim KRQ, Maruyama R, Echigoya Y, Nguyen Q, et al. Inhibition of DUX4 expression with antisense LNA gapmers as a therapy for facioscapulohumeral muscular dystrophy. Proc Natl Acad Sci U S A 2020;117:16509-16515.PMID: 32601200
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