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Amedeo Smart

Independent Medical Education


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Lim KRQ, Maruyama R, Echigoya Y, Nguyen Q, et al. Inhibition of DUX4 expression with antisense LNA gapmers as a therapy for facioscapulohumeral muscular dystrophy. Proc Natl Acad Sci U S A 2020;117:16509-16515.
PMID: 32601200


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