Read + Share

Amedeo Smart

Independent Medical Education


Read + Share

Truong B, Allegri G, Liu XB, Burke KE, et al. Lipid nanoparticle-targeted mRNA therapy as a treatment for the inherited metabolic liver disorder arginase deficiency. Proc Natl Acad Sci U S A 2019;116:21150-21159.
PMID: 31501335


Privacy Policy