In Utero Enzyme-Replacement Therapy for Infantile-Onset Pompe's Disease. Cohen JL, Chakraborty P, Fung-Kee-Fung K, Schwab ME, et al. N Engl J Med 2022 Nov 9. doi: 10.1056/NEJMoa2200587.

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Cohen JL, Chakraborty P, Fung-Kee-Fung K, Schwab ME, et al. In Utero Enzyme-Replacement Therapy for Infantile-Onset Pompe's Disease. N Engl J Med 2022 Nov 9. doi: 10.1056/NEJMoa2200587.
PMID: 36351280